The SMA Victor

Apitegromab is best understood as a muscle-directed therapy. Instead of targeting the SMN1 or SMN2 genes directly, it is designed to inhibit myosta...

One common FAQ regarding SMA progression is: what does “progressive” mean? In Spinal Muscular Atrophy, progression means that motor neurons in the ...

One common FAQ regarding building strength with SMA is: can individuals with SMA safely exercise? The answer depends on the individual’s SMA type, ...

One common FAQ regarding Evrysdi side effects is: what is Evrysdi, and why do side effects matter? Evrysdi, also known as risdiplam, is an FDA-appr...

One common FAQ regarding Evrysdi treatment is: what is Evrysdi, and who is it for? Evrysdi, also known as risdiplam, is an FDA-approved prescriptio...

One common FAQ regarding Zolgensma side effects is: why do side effects matter when discussing SMA treatment? Zolgensma, also known as onasemnogene...

One common FAQ regarding Zolgensma treatment is: what is Zolgensma, and how does it help the SMA community? Zolgensma, also known as onasemnogene a...

One common FAQ regarding Spinraza side effects is: what is Spinraza, and why do side effects matter? Spinraza, also known as nusinersen, is a presc...

One common question in the SMA community is: what is Spinraza treatment? Spinraza, also known as nusinersen, is a prescription medicine used to tre...

For individuals living with SMA, travel can be exciting, meaningful, and empowering, but it can also require far more planning than many people rea...

Breathing problems are the most common cause of illness for adults and children with SMA, and that viral respiratory infections can create severe r...

For students living with SMA, pursuing education can come with challenges that go far beyond homework, tests, and classroom expectations. A student...