The SMA Victor

Because SMA can impact so many areas of daily life, individuals and families often need more than a diagnosis — they need trustworthy resources, me...

SMA is most commonly linked to changes in the SMN1 gene, which reduces the survival motor neuron protein the body needs for healthy motor neurons a...

Apitegromab is best understood as a muscle-directed therapy. Instead of targeting the SMN1 or SMN2 genes directly, it is designed to inhibit myosta...

One common FAQ regarding SMA progression is: what does “progressive” mean? In Spinal Muscular Atrophy, progression means that motor neurons in the ...

One common FAQ regarding building strength with SMA is: can individuals with SMA safely exercise? The answer depends on the individual’s SMA type, ...

One common FAQ regarding Evrysdi side effects is: what is Evrysdi, and why do side effects matter? Evrysdi, also known as risdiplam, is an FDA-appr...

One common FAQ regarding Evrysdi treatment is: what is Evrysdi, and who is it for? Evrysdi, also known as risdiplam, is an FDA-approved prescriptio...

One common FAQ regarding Zolgensma side effects is: why do side effects matter when discussing SMA treatment? Zolgensma, also known as onasemnogene...

One common FAQ regarding Zolgensma treatment is: what is Zolgensma, and how does it help the SMA community? Zolgensma, also known as onasemnogene a...

One common FAQ regarding Spinraza side effects is: what is Spinraza, and why do side effects matter? Spinraza, also known as nusinersen, is a presc...

One common question in the SMA community is: what is Spinraza treatment? Spinraza, also known as nusinersen, is a prescription medicine used to tre...

For individuals living with SMA, travel can be exciting, meaningful, and empowering, but it can also require far more planning than many people rea...